Ascidian Therapeutics

ascidiantx.bsky.social

09 June 2025 17:22

At #CGTP2025 tomorrow, Ascidian’s John Kerwin joins other biotech leaders and gene-editing expert Dr. Kiran Musunuru to discuss the latest advancements in gene editing technologies and their transformative potential for patients. Don’t miss it. #RNAExonEditing #GeneTherapy

American Society of Gene + Cell Therapy

asgct.bsky.social

09 June 2025 17:15

📢 Calling all ASGCT members: Apply for up to nearly $2 million in funded awards through Aug. 1! If you're a researcher growing your career, learn more about our Career Development Award + Underrepresented Populations Fellowship. bit.ly/3TgH54U #genetherapy #celltherapy #careerdevelopment

Christopher Nial

chrisnial.bsky.social

20 May 2025 16:03

Check out my latest article: Gene Therapy: Illuminating a Path for Patients with Rare Diseases www.linkedin.com/pulse/gene-t... via @LinkedIn #GeneTherapy #RareDiseases #HealthcareInnovation #PatientAdvocacy

Logan Thrasher Collins

logantcollins.bsky.social

20 May 2025 16:02

NEJM publication on the demonstration of CRISPR base editing to treat a human infant with a rare genetic disease. As a significant milestone in medicine, this study's results were covered by major news outlets like the New York Times. #genetherapy www.nejm.org/doi/full/10....

National Organization for Rare Disorders (NORD)

nordrare.bsky.social

20 May 2025 16:02

Baby KJ with #CPS1 deficiency was successfully treated using custom #GeneEditing therapy at @childrensphila.bsky.social, a NORD Center of Excellence. Dr. Kiran Musunuru, developer of the #CRISPR #GeneTherapy, will speak at NORD’s Rare Disease Symposium! nordscience.org Read the story: n.pr/3YTUmUx